Pilot Program
Current Grants |
|
Name |
Project Title |
Banfi, Botond, Ph.D. |
Thiocyanate Secretion-Dependent Oxidative Host Defense in CF and Health Airways |
Cornell, Robert, Ph.D. |
Generation of a Transgenic Zebrafish for Optimization of Gene Correction Methodologies |
Keshavje, Shaf, M.D. |
Repair of Damaged Lungs for Transplantation Using and Ex-vivo Gene Therapeutic Surgery |
Raikwar, Sudhanshu, Ph.D. |
Deviation of Insulin-Producing Cells from ES Cells |
Past Grants |
|
Name |
Project Title |
Long Term Gene Expression by Epidermal Stem Cells |
|
Cheng, Pi-Wan, Ph.D. |
Ciliated Cell-Specific Gene Transfer |
Retroviral Gene Transfer to Airway Epithelia with MMLV-based Vectors |
|
Modified Antisense Oligonucleotides as Pseudomonas Antimicrobials |
|
Duan, Dongsheng, Ph.D. |
Analysis of rAAV Integration Specificity |
| Dunnwald, Martine, Ph.D. |
Epidermal Stem Cells as a Gene Delivery System |
Circular Intermediates of rAAV as Novel Gene Transfer Vectors |
|
Gene Transfer into Spiral Ganglion Neurons in vivo |
|
Harper, Scott, Ph.D. |
Autoregulated AAV Vectors for Inducible RNA Interference |
Henry, Michael, Ph.D. |
Cellular Uptake and in vivo Pharmacodynamics of Cholesterol-siRNAs |
Targeted Modulation of Vasopressin in Brain Magnocellular Neurons by Adenovirus-Mediated Gene Therapy |
|
Jones, Bradley, Ph.D. |
Gene Therapy for Phenylketonuria using an Adherent Bacterial Vector |
Kang, Yubin, Ph.D. |
Hematopoietic Stem Cell Gene Transfer for Hemophilia A |
Reversibly Immortal Human Airway Epithelium |
|
Role of CPG Motifs in Plasmid DNA as a Barrier to Gene Transfer |
|
Krieg, Arthur, M.D. |
Development of Non-Immune Activating Gene Therapy Vectors for Cystic Fibrosis |
Site-Directed Mutation of ES Cells by Oligonucleotides |
|
Liang, Luchuan, Ph.D. |
A Study of Epidermal Stem Cells in the Airway |
Adenoviral Mechanisms for Inhibition of Interferon Signal Transduction |
|
Lotery, Andrew, M.D. |
Development of Gene Therapy for Batten Disease |
Zinc Finger Nucleases Targeting Hepatitis B Virus DNAs |
|
Optimization of Retroviral Vectors for Mucosal Delivery |
|
Evaluating Gene Therapy Using a Fluorescent Marker |
|
The CCT Promoter to Drive High-Level Expression of CFTR |
|
AAV-Associated Cluster Contrast Agents for MR/CT Imaging of Vector Biodistribution |
|
Optimization of the CFTR Coding Sequence for Efficient Packaging into the AAV Vector |
|
Reversibly PEGylated Gene Delivery Particles for Treating Cystic Fibrosis |
|
Cell-Specific Targeting of Herpes Simplex Virus in Gene Therapy for Cystic Fibrosis |
|
Sanders, David A, Ph.D. |
Direct Gene Transfer to Intact Airway Epithelia for CF |
Singh, Pradeep, M.D. |
CFTR-Mediatred Gene Correction of Biofilm Formation in the CF Airway |
Targeted Integration of a Lentiviral Vector |
|
A GBV-C Gene Therapy Vector for Cystic Fibrosis |
|
Stecenko, Arlene, M.D. |
Delivery of CFTR Protein Using membrane Translocating Sequences |
Transgene Tolerance: a Role for Apoptosis |
|
Stipp, Christopher, Ph.D. |
Enhancing the Neurite Outgrowth Potential of Neuronal Precursor Cells |
Goblet Cell Hyperplasia and Gene Transfer in CF |
|
Site Directed Mutagenesis Using Triplex Target Sites |
|
Modification of the Cell Surface to Aid Gene Transfer |
|
Harmful Effects of Integrating AAV Vectors |
|
Hybrid rAAV Genomes for Gene Therapy of Cystic Fibrosis |
|
Study of Chimera Recombinant Adenovirus |
|

